Low-density lipoprotein receptor-deficient hepatocytes differentiated from induced pluripotent stem cells allow familial hypercholesterolemia modeling, CRISPR/Cas-mediated genetic correction, and productive hepatitis C virus infection | Stem Cell ...
Targeted Integration and High-Level Transgene Expression in AAVS1 Transgenic Mice after In Vivo HSC Transduction with HDAd5/35++ Vectors: Molecular Therapy
Efficient viral delivery of Cas9 into human safe harbor | Scientific Reports
AAVS1-Targeted Plasmid Integration in AAV Producer Cell Lines | Human Gene Therapy Methods
Quantification of transgene expression in GSH AAVS1 with a novel CRISPR/Cas9-based approach reveals high transcriptional variation: Molecular Therapy - Methods & Clinical Development
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Addgene: AAVS1-Puro-CAG-GCaMP6s
CRISPR Cas9 AAVS1 Safe Harbor Knockin System
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Addgene: AAVS1-EF1a-mTagRFP-T-CAAX
Detection of targeted DSB formation at AAVS1 in HeLa cells. a Target... | Download Scientific Diagram